Abeona Therapeutics Inc.ABEO announced that it has treated the first patient in the pivotal phase III study VIITAL evaluating its lead pipeline candidate, EB-101, in patients with recessive dystrophic epidermolysis bullosa (RDEB). The rare connective tissue disorder, RDEB, is characterized by severe skin wounds and can lead to systemic complications.

The study is being conducted by investigators at Stanford University Medical Center and enrollment in it is ongoing.

Currently, there are no FDA-approved therapies for treating RDEB. A successful development of the gene-corrected cell therapy candidate, EB-101 will be a major boost for the clinical-stage pharma company.

Please note that the company has successfully completed a phase I/II study on EB-101 in RDEB patients. Data from the study showed that treatment with the candidate resulted in sustained and durable wound healing. It also had a favorable safety profile.

Shares of Abeona have lost 37.7% so far this year compared with the industrys decline of 12.7%.

Apart from EB-101, the company has two other clinical-stage pipeline candidates in its portfolio. The candidates ABO-102 and ABO-101 are adeno-associated virus (AAV)-based gene therapies, which are being developed for treating Sanfilippo syndrome type A and Sanfilippo syndrome type B, respectively.

The company is also planning to initiate a phase I/II study to evaluate pre-clinical AAV-based gene therapy candidate, ABO-202 in patients with CLN1 disease soon. An investigational new drug application to support the initiation of the study was approved by the FDA in May 2019.

Abeona Therapeutics Inc. Price

Abeona Therapeutics Inc. Price

Abeona Therapeutics Inc. price | Abeona Therapeutics Inc. Quote

Zacks Rank & Stocks to Consider

Abeona currently has Zacks Rank #3 (Hold) stock.

Some better-ranked stocks from the biotech sector include Regeneron Pharmaceuticals, Inc. REGN, MeiraGTx Holdings PLC MGTX and Verona Pharma PLC VRNA, all sporting a Zacks Rank #1 (Strong Buy). You can seethe complete list of todays Zacks #1 Rank stocks here.

Regenerons earnings estimates for 2020 have gone up from $28.31 to $29.18 and from $28.93 to $30.97 for 2021 over the past 30 days. Regenerons stock has returned 31% so far in 2020.

MeiraGTxs loss estimates for 2020 have narrowed from $2.41 to $2.06 and from $4.10 to $3.40 for 2021 over the past 30 days.

Veronas loss estimates for 2020 have narrowed from $3.95 to $2.65 and from $3.96 to $2.59 for 2021 over the past 30 days.

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Abeona Treats First Patient in Pivotal Gene Therapy Study - Yahoo Finance

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