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Mutant virus used to treat blindness

Scientists have discovered and amplified an evolved adeno-associated virus (AAV) to target and deliver gene therapy to retinal cells in mice. This discovery could lead to less invasive and more precise gene therapies for retinal degeneration diseases such as retinoschisis and Lebers congenital amaurosis, as well as disease in other organs that normally couldnt be treated with gene therapy because of the lack of tissue specific drug delivery systems. This study, which was published in Science Translational Medicine and reported by TheScientist.com, is still in animal trials but has already been praised because of its potential to improve the outcome of gene therapy as well as to expand the use of gene therapy to other diseases.

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