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By its very nature, gene therapy of genetic diseases is a technology of tremendous potential in relieving human suffering, but it is at the same time a massive and dauntingly complex scientific endeavor.

The University of North Carolina School of Medicine created the Gene Therapy Center in 1996 with the goal of merging molecular genetics research with healthcare delivery. The Gene Therapy Center provides important resources to academic investigators through two core facilities created to support preclinical and clinical gene therapy studies.

Lo B, Parham L: Resolving ethical issues in stem cell clinical trials: the example of Parkinson disease. J Law Med Ethics

This article was originally posted on genetherapylive. Cell and gene therapies are currently being evaluated as possible avenues of treatment for multiple inherited retinal diseases in the field of ophthalmology

You should read the following discussion and analysis of our financial conditionand results of operations together with the condensed consolidated financialstatements and related notes that are included elsewhere in this QuarterlyReport on Form 10-Q and our Annual Report on Form 10-K for the fiscal year endedDecember 31, 2019 filed with the U.S. Securities and Exchange Commission, or theSEC, on March 6, 2020, or our 2019 Form 10-K. This discussion containsforward-looking statements based upon current plans, expectations and beliefsthat involve risks and uncertainties

The genetic code to alllife on Earth, both simple and complex, comes down to four basic letters: A, C,T and G. Untangling the role thatthese letters play in lifes blueprint has allowed scientists to understandwhat makes everything from bacteria to people the way they are.

Human beings are a highlyadaptable bunch of bipeds, being able to swiftly change their lifestyles, clothes, hair, chewing gum brands, and political opinionsas the wind blows.But none of us are capable of intentionally altering our own genetic code as this superpowered species ofsquid has demonstrated! In what could one day be used to affect gene-editing medicines and therapies to cure diseases in people, a new research paper publishedthis weekin the onlinejournalNucleic Acids Researchpresents evidence that a particular species of longfin inshore squid (Doryteuthis pealeii), commonly used as bait fish, isthe first-ever animal known to changemessenger RNAoutside of the cell nucleus.Most all creatures on this planet enact changes to their DNA from the cell nucleus via messenger RNA, but this crafty little oceanic creature takes a unique shortcut. Scientists working out of the famous Woods HoleMarine Biological Laboratory inMassachusetts found that this extreme RNA editing process occurs withinthe squid on a fantasticscale, using over60,000 brain cells, and dwarfing the hundreds of similar sites registering in humans

Although anti-CD19 chimeric antigen receptor T-cell (CAR-T)therapy has led to dramatic results in patients with hematological malignancieswho are seemingly out of treatment options, it is far from a panacea for allpatients, as a meaningful portion have disease that either never responds toCAR-T or eventually comes back after treatment with CAR-T.

On August 23, 2019, the FamilieSCN2A Foundation held their biennial SCN2A Professional and Family meeting, in Seattle, Washington. The gathering brought together 37 families of individuals with mutations in the SCN2A gene, 60 investigators, eight clinicians and five industry groups that conduct research and/or clinical work on conditions related to this genetic change. A number of SFARI scientists and staff also attended the event

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Dr. Edmund Chein, M.D., author of Age Reversal, Bio-Identical Hormones and Telomerase, and Living to 120 and Beyond, has appeared on various radio and television shows such as: Dr. Chein is a practicing physician in Palm Springs, California who is regarded by many as one of the founding fathers of longevity and anti-aging medicine.Today, he is known as one of the best bioidentical hormone doctors in the world.

"The event reflected the fantastic growing enthusiasm around cell and gene therapy, including small and large companies, investors and regulators. It was great to see everyone so engaged and so positive. The event really gives you the pulse of what is happening right now in cell and gene therapy." Vice President, Regulatory Science, Bluebird Bio, Inc Great program, great people, great venue

ANI | Washington D.C. [USA] June 11, 2017 Last Updated at 13:42 IST Glucocorticoid steroids, such as prednisone, may improve effectiveness of AAV-based gene therapy by reducing immune response, according to a recent research.

VANCOUVER, BRITISH COLUMBIA--(Marketwired - March 13, 2017) - NOT FOR DISSEMINATION IN THE UNITED STATES Editors Note: There is a photo associated with this press release. Woodrose Ventures Corporation (TSX VENTURE:WRS.H) ("Woodrose" or the "Company") is pleased to announce that it has entered into an agreement (the "Agreement") dated March 10, 2017 to acquire all of the shares of Novoheart Holdings Ltd. ("Novoheart"), a global stem cell biotechnology company dedicated to human heart engineering (the "Transaction")

A treatment for Cystic Fibrosis.

Researchers have been working for decades to bring gene therapy to the clinic, yet very few patients have received any effective gene-therapy treatments. But that doesn't mean gene therapy is an impossible dream

USFWS Fisheries posted a photo: Fish Biologist Kevin Pankow, from the Green Bay Fish and Wildlife Conservation Office (FWCO), assisted the Michigan Department of Natural Resources (DNR), NOAA Northwest Fisheries Science Center, Ashland Fish and Wildlife Conservation Office, National Park Service and University of Wisconsin-Milwaukee the week of June 2, 2014 with a lake trout research project near Isle Royale National Park on Lake Superior. The cooperative, 2-year research project, coauthored by Chuck Bronte from Green Bay FWCO, was funded by a competitive grant from the Great Lakes Fishery Commission. The objectives of the project are to characterize the seasonal reproductive development, assess the genetic relatedness of individuals within a given morphotype collected seasonally to determine if they are derived from the same morphotype populations, and compare fecundity and skeletal muscle lipid levels among lean, siscowet, humper and redfin lake trout at Isle Royale.

Contributed By: Dave Blanchard OPB | May 22, 2014 12:06 p.m.

Theme: Uncover the potential that lies within the cell Zhe Sha, Harvard Medical School, USA Its my real honor to be part of this great conference. I had a truly rewarding experience meeting with many experts in the field.

Gene therapy is an experimental technique that uses genes to treat or prevent disease. In the future, this technique may allow doctors to treat a disorder by inserting a gene into a patients cells instead of using drugs or surgery

26.09.2013 - (idw) Universitt Konstanz ERC Advanced Grant for the chemist Professor Dr. Andreas Marx from Konstanz for research on gene modification The chemist Professor Dr